About the Authors
- Palittiya Sintusek
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Affiliations Dubowitz Neuromuscular Centre, Institute of Child Health, University College London, London, United Kingdom, Division of Gastroenterology and Hepatology, Department of Pediatrics, Faculty of Medicine, King Chulalongkorn Memorial Hospital, Chulalongkorn University, Bangkok, Thailand
- Francesco Catapano
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Affiliation Dubowitz Neuromuscular Centre, Institute of Child Health, University College London, London, United Kingdom
- Napat Angkathunkayul
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Affiliation Department of Pathology, Ramathibodi Hospital, Mahidol University, Bangkok, Thailand
- Elena Marrosu
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Affiliation Dubowitz Neuromuscular Centre, Institute of Child Health, University College London, London, United Kingdom
- Simon H. Parson
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Affiliations Institute of Medical Sciences, University of Aberdeen, Foresterhill, Aberdeen, United Kingdom, Euan MacDonald Center for Motor Neuron Disease Research, University of Edinburgh, Edinburgh, United Kingdom
- Jennifer E. Morgan
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Affiliation Dubowitz Neuromuscular Centre, Institute of Child Health, University College London, London, United Kingdom
- Francesco Muntoni
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* E-mail: Haiyan.zhou@ucl.ac.uk (HZ); f.muntoni@ucl.ac.uk (FM)
Affiliation Dubowitz Neuromuscular Centre, Institute of Child Health, University College London, London, United Kingdom
- Haiyan Zhou
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* E-mail: Haiyan.zhou@ucl.ac.uk (HZ); f.muntoni@ucl.ac.uk (FM)
Affiliation Dubowitz Neuromuscular Centre, Institute of Child Health, University College London, London, United Kingdom
Competing Interests
FM is involved as a principal investigator in SMA clinical trials in collaboration with Ionis and Biogen, and Roche. He is also member of the Scientific Advisory Board of the Rare Disease section at Pfizer. This does not alter our adherence to PLOS ONE policies on sharing data and materials. The remaining authors disclose no conflicts.
Author Contributions
Conceived and designed the experiments: HZ FM. Performed the experiments: HZ PS FC EM. Analyzed the data: HZ PS NA. Wrote the paper: HZ PS JEM SHP FM.