About the Authors
- Calogera M. Simonaro
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* E-mail: calogera.simonaro@mssm.edu
Affiliation Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, NY, United States of America
- Shunji Tomatsu
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Affiliation Skeletal Dysplasia Laboratory, Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, United States of America
- Tracy Sikora
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Affiliation School of Veterinary Medicine, University of Pennsylvania, Philadelphia, PA, United States of America
- Francyne Kubaski
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Affiliation Skeletal Dysplasia Laboratory, Nemours/Alfred I. duPont Hospital for Children, Wilmington, DE, United States of America
- Michael Frohbergh
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Affiliation Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, NY, United States of America
- Johana M. Guevara
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Affiliations Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, NY, United States of America, Pontificia Universidad Javeriana, Bogota, Colombia
- Raymond Y. Wang
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Affiliations Division of Metabolic Disorders, Children’s Hospital of Orange County, Orange, CA, United States of America, Division of Medical Genetics, Department of Pediatrics, Harbor-UCLA Medical Center, Torrance, CA, United States of America
- Moin Vera
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Affiliation Division of Metabolic Disorders, Children’s Hospital of Orange County, Orange, CA, United States of America
- Jennifer L. Kang
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Affiliation Department of Neurosurgery, University of Pennsylvania, Philadelphia, PA, United States of America
- Lachlan J. Smith
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Affiliation Department of Neurosurgery, University of Pennsylvania, Philadelphia, PA, United States of America
- Edward H. Schuchman
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Affiliation Department of Genetics and Genomic Sciences, Icahn School of Medicine at Mount Sinai, New York, NY, United States of America
- Mark E. Haskins
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Affiliation School of Veterinary Medicine, University of Pennsylvania, Philadelphia, PA, United States of America
Competing Interests
A patent has been filed "Anti-TNF therapy for the mucopolysaccharidoses and other lysosomal storage diseases" (PCT/US2012/043369,WO2012177778) by Drs. Simonaro and Schuchman. This patent has not as yet been awarded. This does not alter the authors’ adherence to all PLOS ONE policies on sharing data and materials.
Author Contributions
Conceived and designed the experiments: CMS EHS MEH. Performed the experiments: CMS EHS MEH ST TS FK MF JMG LJS RYW MV JLK. Analyzed the data: CMS EHS MEH ST LJS RYW. Contributed reagents/materials/analysis tools: CMS EHS MEH ST LJS. Wrote the paper: CMS EHS MEH.