About the Authors

Fernanda dos Santos Pereira

Affiliations Gene Therapy Center, Hospital de Clínicas de Porto Alegre, Porto Alegre, Brazil, Post-Graduation Program in Medical Sciences, Universidade Federal do Rio Grande do Sul, Porto Alegre, Brazil

Ursula Matte

Affiliations Gene Therapy Center, Hospital de Clínicas de Porto Alegre, Porto Alegre, Brazil, Post-Graduation Program in Genetics and Molecular Biology, Universidade Federal do Rio Grande do Sul, Porto Alegre, Brazil

Clarissa Troller Habekost

Affiliations Medical Genetics Service, Hospital de Clínicas de Porto Alegre, Porto Alegre, Brazil, Post-Graduation Program in Genetics and Molecular Biology, Universidade Federal do Rio Grande do Sul, Porto Alegre, Brazil

Raphael Machado de Castilhos

Affiliations Medical Genetics Service, Hospital de Clínicas de Porto Alegre, Porto Alegre, Brazil, Post-Graduation Program in Medical Sciences, Universidade Federal do Rio Grande do Sul, Porto Alegre, Brazil

Antonette Souto El Husny

Affiliation Medical Genetics Service, Hospital de Clínicas de Porto Alegre, Porto Alegre, Brazil

Charles Marques Lourenço

Affiliation Hospital de Clinicas de Ribeirão Preto, Universidade de São Paulo, São Paulo, Brazil

Angela M. Vianna-Morgante

Affiliation Department of Genetics and Evolutionary Biology, Institute of Biosciences, Universidade de São Paulo, São Paulo, Brazil

Liane Giuliani

Affiliation Department of Pediatrics, Universidade Federal do Mato Grosso do Sul, Campo Grande, Brazil

Marcial Francis Galera

Affiliation School of Medicine, Universidade de Cuiabá, Cuiabá, Brazil

Rachel Honjo

Affiliation Department of Genetics, Children Institute, Universidade de São Paulo, São Paulo, Brazil

Chong Ae Kim

Affiliation Department of Genetics, Children Institute, Universidade de São Paulo, São Paulo, Brazil

Juan Politei

Affiliation Neuromuscular Disorders and Neuropathic Pain Section, Neurology Department, Hospital Juan A. Fernández, Buenos Aires, Argentina

Carmen Regla Vargas

Affiliations Medical Genetics Service, Hospital de Clínicas de Porto Alegre, Porto Alegre, Brazil, Department of Analysis, Universidade Federal do Rio Grande do Sul, Porto Alegre, Brazil

Laura Bannach Jardim

ljardim@hcpa.ufrgs.br

Affiliations Medical Genetics Service, Hospital de Clínicas de Porto Alegre, Porto Alegre, Brazil, Post-Graduation Program in Medical Sciences, Universidade Federal do Rio Grande do Sul, Porto Alegre, Brazil, Post-Graduation Program in Genetics and Molecular Biology, Universidade Federal do Rio Grande do Sul, Porto Alegre, Brazil, Department of Internal Medicine, Universidade Federal do Rio Grande do Sul, Porto Alegre, Brazil

Competing Interests

The authors have declared that no competing interests exist.

Author Contributions

Conceived and designed the experiments: FSP UM LBJ. Performed the experiments: FSP UM. Analyzed the data: UM CTH LBJ. Contributed reagents/materials/analysis tools: RMC ASEH CML AMV-M LG MFG RH CAK JP CRV LBJ. Wrote the paper: FSP UM LBJ.