About the Authors
- Thomas O. Crawford
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* E-mail: tcrawfo@jhmi.edu
Affiliation Departments of Neurology and Pediatrics, The Johns Hopkins University, Baltimore, Maryland, United States of America
- Sergey V. Paushkin
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Affiliation Spinal Muscular Atrophy Foundation, New York, New York, United States of America
- Dione T. Kobayashi
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Affiliation Spinal Muscular Atrophy Foundation, New York, New York, United States of America
- Suzanne J. Forrest
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Affiliation Spinal Muscular Atrophy Foundation, New York, New York, United States of America
- Cynthia L. Joyce
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Affiliation Spinal Muscular Atrophy Foundation, New York, New York, United States of America
- Richard S. Finkel
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Affiliation Departments of Neurology and Pediatrics, Children’s Hospital of Philadelphia and University of Pennsylvania School of Medicine, Philadelphia, Pennsylvania, United States of America
- Petra Kaufmann
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Affiliation Department of Neurology, Columbia University, New York, New York, United States of America
- Kathryn J. Swoboda
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Affiliation Departments of Neurology and Pediatrics, University of Utah School of Medicine, Salt Lake City, Utah, United States of America
- Danilo Tiziano
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Affiliation Instituto di Genetica Medica, Università Cattolica S. Cuore, Roma, Italy
- Rosa Lomastro
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Affiliation Instituto di Genetica Medica, Università Cattolica S. Cuore, Roma, Italy
- Rebecca H. Li
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Affiliation New England Research Institutes, Inc., Watertown, Massachusetts, United States of America
- Felicia L. Trachtenberg
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Affiliation New England Research Institutes, Inc., Watertown, Massachusetts, United States of America
- Thomas Plasterer
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Affiliation Department of Chemistry and Chemical Biology, Northeastern University, Boston, Massachusetts, United States of America
- Karen S. Chen
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Affiliation Spinal Muscular Atrophy Foundation, New York, New York, United States of America
- on behalf of the Pilot Study of Biomarkers for Spinal Muscular Atrophy (BforSMA) Trial Group
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¶Members of the BforSMA Trial Group are listed in
List S1 .
Competing Interests
See below for the Full List of Competing Interests.
Author Contributions
Conceived and designed the experiments: TOC SVP DTK SJF CLJ RSF PK KJS RL KSC. Performed the experiments: TOC DTK RSF PK KJS RHL. Analyzed the data: TOC SVP SJF CLJ RSF PK KJS DT RHL FLT TP KSC. Contributed reagents/materials/analysis tools: DT TP. Wrote the paper: TOC SVP DTK SJF CLJ RSF KJS TP KSC.