About the Authors

Weidong Xiong

Contributed equally to this work with: Weidong Xiong, Marianela Candolfi

Affiliation Gene Therapeutics Research Institute, Cedars-Sinai Medical Center and Department of Medicine and Department of Molecular and Medical Pharmacology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

Marianela Candolfi

Contributed equally to this work with: Weidong Xiong, Marianela Candolfi

Affiliation Gene Therapeutics Research Institute, Cedars-Sinai Medical Center and Department of Medicine and Department of Molecular and Medical Pharmacology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

Chunyan Liu

Affiliation Gene Therapeutics Research Institute, Cedars-Sinai Medical Center and Department of Medicine and Department of Molecular and Medical Pharmacology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

A. K. M. Ghulam Muhammad

Affiliation Gene Therapeutics Research Institute, Cedars-Sinai Medical Center and Department of Medicine and Department of Molecular and Medical Pharmacology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

Kader Yagiz

Affiliation Gene Therapeutics Research Institute, Cedars-Sinai Medical Center and Department of Medicine and Department of Molecular and Medical Pharmacology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

Mariana Puntel

Affiliation Gene Therapeutics Research Institute, Cedars-Sinai Medical Center and Department of Medicine and Department of Molecular and Medical Pharmacology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

Peter F. Moore

Affiliation Pathology, Microbiology, and Immunology, School of Veterinary Medicine, University of California Davis, Davis, California, United States of America

Julie Avalos

Affiliation Department of Comparative Medicine, Cedars-Sinai Medical Center, Los Angeles, California, United States of America

John D. Young

Affiliation Department of Comparative Medicine, Cedars-Sinai Medical Center, Los Angeles, California, United States of America

Dorothy Khan

Affiliation Department of Comparative Medicine, Cedars-Sinai Medical Center, Los Angeles, California, United States of America

Randy Donelson

Affiliation Department of Pediatrics, University of Minnesota, Minneapolis, Minnesota, United States of America

G. Elizabeth Pluhar

Affiliation Department of Small Animal Clinical Sciences, University of Minnesota, St. Paul, Minnesota, United States of America

John R. Ohlfest

Affiliations Department of Pediatrics, University of Minnesota, Minneapolis, Minnesota, United States of America, Department of Neurosurgery, University of Minnesota, Minneapolis, Minnesota, United States of America

Kolja Wawrowsky

Affiliation Department of Medicine, Cedars-Sinai Medical Center and David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

Pedro R. Lowenstein

Affiliation Gene Therapeutics Research Institute, Cedars-Sinai Medical Center and Department of Medicine and Department of Molecular and Medical Pharmacology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

Maria G. Castro

castromg@cshs.org

Affiliation Gene Therapeutics Research Institute, Cedars-Sinai Medical Center and Department of Medicine and Department of Molecular and Medical Pharmacology, David Geffen School of Medicine, University of California Los Angeles, Los Angeles, California, United States of America

Competing Interests

The authors have declared that no competing interests exist.

Author Contributions

Conceived and designed the experiments: PRL MGC. Performed the experiments: WdX MC CL AGM KY MP PFM JA JDY DK RD JRO GEP KW. Analyzed the data: WdX MC CL AGM KY MP JA JDY DK RD JRO GEP KW PRL MGC. Contributed reagents/materials/analysis tools: PFM JA JDY DK RD JRO GEP. Wrote the paper: WdX MC PRL MGC.