About the Authors
- Steven M. Rowe
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Affiliation University of Alabama at Birmingham, Birmingham, Alabama, United States of America
- Bo Liu
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Affiliation University of Alabama at Birmingham, Birmingham, Alabama, United States of America
- Aubrey Hill
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Affiliation University of Alabama at Birmingham, Birmingham, Alabama, United States of America
- Heather Hathorne
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Affiliation University of Alabama at Birmingham, Birmingham, Alabama, United States of America
- Morty Cohen
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Current address: Morty Cohen Research Consulting, Seattle, Washington, United States of America
Affiliation Seattle Children's Hospital, Seattle, Washington, United States of America
- John R. Beamer
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Current address: ALK Source Materials, Inc., Post Falls, Idaho, United States of America
Affiliation Seattle Children's Hospital, Seattle, Washington, United States of America
- Frank J. Accurso
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Affiliation University of Colorado Denver, Aurora, Colorado, United States of America
- Qunming Dong
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Affiliation Vertex Pharmaceuticals Incorporated, Cambridge, Massachusetts, United States of America
- Claudia L. Ordoñez
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Current address: Biogen, Boston, Massachusetts, United States of America
Affiliation Vertex Pharmaceuticals Incorporated, Cambridge, Massachusetts, United States of America
- Anne J. Stone
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Affiliation Vertex Pharmaceuticals Incorporated, Cambridge, Massachusetts, United States of America
- Eric R. Olson
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Affiliation Vertex Pharmaceuticals Incorporated, Cambridge, Massachusetts, United States of America
- John P. Clancy
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* E-mail: john.clancy@cchmc.org
Affiliation Cincinnati Children's Hospital Medical Center and the University of Cincinnati, Cincinnati, Ohio, United States of America
- for the VX06-770-101 Study Group
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¶Membership of the VX06-770-101 Study Group is provided in the Acknowledgments.
Competing Interests
Several authors on this manuscript are (or were) employees of Vertex Pharmaceuticals (QD, CLO, AJS, and ERO), Drs. JPC, FJA, and SMR were site investigators for the primary study of interest that was funded by Vertex Pharmaceuticals, and Dr. JPC has served as a consultant for Vertex Pharmaceuticals (member of the CF Global Scientific Advisory Board). This does not alter the authors' adherence to all of the PLOS ONE policies on sharing data and materials.
Author Contributions
Conceived and designed the experiments: SMR MC JB FJA CLO ERO JPC. Performed the experiments: SMR HH MC FJA JPC. Analyzed the data: SMR BL AH QD AJS JPC. Contributed reagents/materials/analysis tools: BL AH. Wrote the paper: SMR FJA QD JPC.