About the Authors
- You-Hai Xu
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Affiliations Division of Human Genetics, Cincinnati Children's Hospital Research Foundation, Cincinnati, Ohio, United States of America, Department of Pediatrics, University of Cincinnati, Cincinnati, Ohio, United States of America
- Ying Sun
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Affiliations Division of Human Genetics, Cincinnati Children's Hospital Research Foundation, Cincinnati, Ohio, United States of America, Department of Pediatrics, University of Cincinnati, Cincinnati, Ohio, United States of America
- Sonya Barnes
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Affiliation Division of Human Genetics, Cincinnati Children's Hospital Research Foundation, Cincinnati, Ohio, United States of America
- Gregory A. Grabowski
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* E-mail: greg.grabowski@cchmc.org
Affiliations Division of Human Genetics, Cincinnati Children's Hospital Research Foundation, Cincinnati, Ohio, United States of America, Department of Pediatrics, University of Cincinnati, Cincinnati, Ohio, United States of America
Competing Interests
The Drs. Xu, Sun and Barnes declare no conflicting financial interests. Dr. Grabowski is a paid consultant for and has research grants for basic research from the Genzyme Corp. and Shire Human Genetic Therapies. In addition, he received honoraria from Genzyme Corp. and Shire Human Genetic Therapies for speaking engagements. The Shire Human Genetic Therapies funded this work, but had no role in study design, data collection and analysis, decision to publish, or preparation of the manuscript.
Author Contributions
Conceived and designed the experiments: YHX YS SB GG. Performed the experiments: YHX YS SB GG. Analyzed the data: YHX YS GG. Wrote the paper: YHX YS SB GG.