Download Citation
Article Source:
Phase 2a Study of Ataluren-Mediated Dystrophin Production in Patients with Nonsense Mutation Duchenne Muscular Dystrophy
Finkel RS,
Flanigan KM,
Wong B,
Bönnemann C,
Sampson J,
et al.
(2013)
Phase 2a Study of Ataluren-Mediated Dystrophin Production in Patients with Nonsense Mutation Duchenne Muscular Dystrophy.
PLOS ONE 8(12): e81302.
https://doi.org/10.1371/journal.pone.0081302