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Open Access
Peer-reviewed
Research Article
A G542X cystic fibrosis mouse model for examining nonsense mutation directed therapies
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Daniel R. McHugh,
Roles Conceptualization, Data curation, Formal analysis, Investigation, Methodology, Validation, Writing – original draft, Writing – review & editing
Affiliations Department of Genetics and Genome Sciences, Case Western Reserve University, Cleveland, Ohio, United States of America, Department of Pediatrics, Case Western Reserve University, Cleveland, Ohio, United States of America
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Miarasa S. Steele,
Roles Investigation, Validation, Writing – review & editing
Affiliation Department of Pediatrics, Case Western Reserve University, Cleveland, Ohio, United States of America
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Dana M. Valerio,
Roles Data curation, Investigation, Writing – review & editing
Affiliation Department of Pediatrics, Case Western Reserve University, Cleveland, Ohio, United States of America
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Alexander Miron,
Roles Data curation, Formal analysis, Writing – review & editing
Affiliation Department of Genetics and Genome Sciences, Case Western Reserve University, Cleveland, Ohio, United States of America
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Rachel J. Mann,
Roles Data curation, Investigation, Writing – review & editing
Affiliation Department of Genetics and Genome Sciences, Case Western Reserve University, Cleveland, Ohio, United States of America
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David F. LePage,
Roles Data curation, Formal analysis, Investigation, Writing – review & editing
Affiliation Department of Genetics and Genome Sciences, Case Western Reserve University, Cleveland, Ohio, United States of America
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Ronald A. Conlon,
Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Supervision, Writing – review & editing
Affiliation Department of Genetics and Genome Sciences, Case Western Reserve University, Cleveland, Ohio, United States of America
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Calvin U. Cotton,
Roles Formal analysis, Investigation, Methodology, Resources, Writing – review & editing
Affiliations Department of Pediatrics, Case Western Reserve University, Cleveland, Ohio, United States of America, Department of Physiology and Biophysics, Case Western Reserve University, Cleveland, Ohio, United States of America
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Mitchell L. Drumm,
Roles Formal analysis, Resources, Supervision, Writing – review & editing
Affiliations Department of Genetics and Genome Sciences, Case Western Reserve University, Cleveland, Ohio, United States of America, Department of Pediatrics, Case Western Reserve University, Cleveland, Ohio, United States of America
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Craig A. Hodges
Roles Conceptualization, Data curation, Formal analysis, Funding acquisition, Investigation, Methodology, Project administration, Resources, Supervision, Validation, Writing – original draft, Writing – review & editing
* E-mail: craig.hodges@case.edu
Affiliations Department of Genetics and Genome Sciences, Case Western Reserve University, Cleveland, Ohio, United States of America, Department of Pediatrics, Case Western Reserve University, Cleveland, Ohio, United States of America
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A G542X cystic fibrosis mouse model for examining nonsense mutation directed therapies
- Daniel R. McHugh,
- Miarasa S. Steele,
- Dana M. Valerio,
- Alexander Miron,
- Rachel J. Mann,
- David F. LePage,
- Ronald A. Conlon,
- Calvin U. Cotton,
- Mitchell L. Drumm,
- Craig A. Hodges
- Published: June 20, 2018
- https://doi.org/10.1371/journal.pone.0199573