About the Authors

Jennifer E. Chung

Contributed equally to this work with: Jennifer E. Chung, Wendy Magis

Roles Formal analysis, Investigation, Writing – original draft

Affiliation Innovative Genomics Institute, University of California, Berkeley, CA, United States of America

Wendy Magis

Contributed equally to this work with: Jennifer E. Chung, Wendy Magis

Roles Formal analysis, Investigation

Affiliation Children’s Hospital Oakland Research Institute, UCSF Benioff Children’s Hospital, Oakland, CA, United States of America

Jonathan Vu

Roles Investigation, Methodology

Affiliation Innovative Genomics Institute, University of California, Berkeley, CA, United States of America

Seok-Jin Heo

Roles Formal analysis, Investigation, Methodology, Resources

Affiliation Children’s Hospital Oakland Research Institute, UCSF Benioff Children’s Hospital, Oakland, CA, United States of America

Kirmo Wartiovaara

Roles Conceptualization

Affiliations Children’s Hospital Oakland Research Institute, UCSF Benioff Children’s Hospital, Oakland, CA, United States of America, Research Programs Unit, Molecular Neurology and Biomedicum Stem Cell Centre, Faculty of Medicine, University of Helsinki, Helsinki, Finland, Clinical Genetics, HUSLAB, Helsinki University Central Hospital, Helsinki, Finland

Mark C. Walters

Roles Conceptualization, Writing – review & editing

Affiliations Children’s Hospital Oakland Research Institute, UCSF Benioff Children’s Hospital, Oakland, CA, United States of America, Blood and Marrow Transplant Program, Division of Hematology, UCSF Benioff Children’s Hospital, Oakland, CA, United States of America

Ryo Kurita

Roles Resources

Affiliation Cell Engineering Division, RIKEN BioResource Center, Tsukuba, Ibaraki, Japan

Yukio Nakamura

Roles Resources

Affiliations Cell Engineering Division, RIKEN BioResource Center, Tsukuba, Ibaraki, Japan, Faculty of Medicine, University of Tsukuba, Tsukuba, Ibaraki, Japan

Dario Boffelli

Roles Data curation, Formal analysis, Project administration, Writing – review & editing

Affiliation Children’s Hospital Oakland Research Institute, UCSF Benioff Children’s Hospital, Oakland, CA, United States of America

David I. K. Martin

Roles Conceptualization, Formal analysis, Investigation, Methodology, Project administration, Supervision, Writing – original draft, Writing – review & editing

dewittm@berkeley.edu (MAD); jcorn@berkeley.edu (JEC); dimartin@chori.org (DIKM)

Affiliation Children’s Hospital Oakland Research Institute, UCSF Benioff Children’s Hospital, Oakland, CA, United States of America

Jacob E. Corn

Roles Data curation, Funding acquisition, Methodology, Project administration, Resources, Supervision, Writing – review & editing

dewittm@berkeley.edu (MAD); jcorn@berkeley.edu (JEC); dimartin@chori.org (DIKM)

Affiliations Innovative Genomics Institute, University of California, Berkeley, CA, United States of America, Department of Molecular and Cellular Biology, University of California, Berkeley, CA, United States of America

Mark A. DeWitt

Roles Data curation, Formal analysis, Investigation, Methodology, Project administration, Supervision, Visualization, Writing – original draft, Writing – review & editing

dewittm@berkeley.edu (MAD); jcorn@berkeley.edu (JEC); dimartin@chori.org (DIKM)

Affiliation Innovative Genomics Institute, University of California, Berkeley, CA, United States of America

Competing Interests

The authors have declared that no competing interests exist.