About the Authors
- Aurélie Chabanon
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Roles Data curation, Methodology, Project administration, Visualization, Writing – original draft, Writing – review & editing
Affiliation Institute of Myology, GH Pitié Salpêtrière, Paris, France
- Andreea Mihaela Seferian
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Roles Investigation, Resources, Writing – review & editing
Affiliation Institute of Myology, GH Pitié Salpêtrière, Paris, France
- Aurore Daron
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Roles Investigation, Resources, Writing – review & editing
Affiliation Centre de Référence des Maladies Neuromusculaires, CHU de Liège, Belgium
- Yann Péréon
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Roles Investigation, Resources, Writing – review & editing
Affiliation Centre de Référence Maladies Neuromusculaires Atlantique-Occitanie-Caraïbes, Hôpital Hôtel-Dieu, Nantes, France
- Claude Cances
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Roles Investigation, Resources, Writing – review & editing
Affiliations Centre de Référence des Maladies Neuromusculaires, Hôpital des Enfants, Toulouse, France, Unité de neurologie pédiatrique, Hôpital des Enfants, Toulouse, France
- Carole Vuillerot
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Roles Investigation, Resources, Writing – review & editing
Affiliation Service de rééducation pédiatrique infantile”L’Escale”, Hôpital Mère Enfant, CHU-Lyon, Lyon, France
- Liesbeth De Waele
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Roles Investigation, Resources, Writing – review & editing
Affiliations Department of Pediatric Neurology, University Hospitals Leuven, Leuven, Belgium, Department of Development and Regeneration, KU Leuven Kulak Kortijk, Kortrijk, Belgium
- Jean-Marie Cuisset
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Roles Investigation, Resources, Writing – review & editing
Affiliations Centre de Référence des Maladies Neuromusculaires, Hôpital Roger Salengro, Lille, France, Service de Neuropédiatrie, Hôpital Roger Salengro, Lille, France
- Vincent Laugel
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Roles Investigation, Resources, Writing – review & editing
Affiliation Neuropédiatrie/INSERM CIC 1434, CHU Strasbourg Hautepierre, Strasbourg, France
- Ulrike Schara
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Roles Investigation, Resources, Writing – review & editing
Affiliation Paediatric neurology and neuromuscular center, University of Essen, Essen, Germany
- Teresa Gidaro
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Roles Investigation, Resources, Writing – review & editing
Affiliation Institute of Myology, GH Pitié Salpêtrière, Paris, France
- Stéphanie Gilabert
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Roles Investigation, Writing – review & editing
Affiliation Institute of Myology, GH Pitié Salpêtrière, Paris, France
- Jean-Yves Hogrel
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Roles Conceptualization, Data curation, Methodology, Resources, Writing – review & editing
Affiliation Institute of Myology, GH Pitié Salpêtrière, Paris, France
- Pierre-Yves Baudin
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Roles Resources
Affiliation Consultants for Research in Imaging and Spectroscopy (CRIS), Tournai, Belgium
- Pierre Carlier
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Roles Investigation, Methodology, Resources, Writing – review & editing
Affiliation Institute of Myology, GH Pitié Salpêtrière, Paris, France
- Emmanuel Fournier
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Roles Data curation, Investigation, Methodology, Writing – review & editing
Affiliation Institute of Myology, GH Pitié Salpêtrière, Paris, France
- Linda Pax Lowes
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Roles Data curation, Methodology, Resources, Writing – review & editing
Affiliation Center for Gene Therapy, Nationwide Children's Hospital, Columbus, Ohio, USA
- Nicole Hellbach
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Roles Methodology, Resources, Writing – review & editing
Affiliation Roche Pharmaceutical Research and Early Development, Roche Innovation Center, Basel, Switzerland
- Timothy Seabrook
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Roles Conceptualization, Funding acquisition, Methodology, Supervision, Writing – review & editing
Affiliation Roche Pharmaceutical Research and Early Development, Roche Innovation Center, Basel, Switzerland
- Elie Toledano
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Roles Conceptualization, Funding acquisition, Methodology, Supervision, Writing – review & editing
Affiliation Institut Roche, Paris, France
- Mélanie Annoussamy
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Roles Conceptualization, Formal analysis, Funding acquisition, Methodology, Project administration, Supervision, Writing – review & editing
Affiliation Institute of Myology, GH Pitié Salpêtrière, Paris, France
- Laurent Servais
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Roles Conceptualization, Funding acquisition, Investigation, Methodology, Resources, Supervision, Writing – review & editing
* E-mail: l.servais@institut-myologie.org
Affiliations Institute of Myology, GH Pitié Salpêtrière, Paris, France, Centre de Référence des Maladies Neuromusculaires, CHU de Liège, Belgium, Service de Pédiatrie, CHU de Liège, Liège, Belgium
- the NatHis-SMA study group
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¶Membership of the NatHis-SMA study group is provided in the Acknowledgments.
Competing Interests
CV has received travel grants from Allergan and Roche for participation at meetings and has consultancy activities for Biogen and F. Hoffmann-La Roche; LV has served on scientific advisory board for Biogen and F. Hoffmann-La Roche; US has served on scientific advisory boards for Biogen, Novartis and F. Hoffmann-La Roche; JYH is co-inventor of the MyoGrip and MyoPinch devices; JYH and LS are co-inventors of the MoviPlate device; LPL is co-inventor of the ACTIVE system; PYB is employee of CRIS; TS, NH and ET are employees of Roche Group; LS is co-inventor of the ActiMyo device and has served on scientific advisory boards for AveXis, Biogen and F. Hoffmann-La Roche. This does not alter our adherence to PLOS ONE policies on sharing data and materials.