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Open Access
Peer-reviewed
Research Article
Oral tetrahydrouridine and decitabine for non-cytotoxic epigenetic gene regulation in sickle cell disease: A randomized phase 1 study
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Robert Molokie,
Roles Investigation, Methodology, Project administration, Supervision, Validation, Writing – review & editing
Affiliations Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America, Jesse Brown VA Medical Center, Chicago, Illinois, United States of America
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Donald Lavelle,
Roles Formal analysis, Investigation, Methodology, Supervision, Validation, Writing – review & editing
Affiliations Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America, Jesse Brown VA Medical Center, Chicago, Illinois, United States of America
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Michel Gowhari,
Roles Investigation, Project administration, Supervision, Writing – review & editing
Affiliation Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America
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Michael Pacini,
Roles Investigation, Methodology, Project administration, Supervision, Writing – review & editing
Affiliation Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America
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Lani Krauz,
Roles Data curation, Methodology, Project administration, Supervision, Writing – review & editing
Affiliation Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America
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Johara Hassan,
Roles Investigation, Project administration, Supervision, Writing – review & editing
Affiliation Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America
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Vinzon Ibanez,
Roles Formal analysis, Investigation, Writing – review & editing
Affiliation Jesse Brown VA Medical Center, Chicago, Illinois, United States of America
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Maria A. Ruiz,
Roles Formal analysis, Investigation, Writing – review & editing
Affiliation Jesse Brown VA Medical Center, Chicago, Illinois, United States of America
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Kwok Peng Ng,
Roles Formal analysis, Investigation, Writing – review & editing
Affiliation Translational Hematology and Oncology Research, Taussig Cancer Institute, Cleveland Clinic, Cleveland, Ohio, United States of America
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Philip Woost,
Roles Formal analysis, Investigation, Validation, Writing – review & editing
Affiliation Case Comprehensive Cancer Center, Case Western Reserve University, Cleveland, Ohio, United States of America
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Tomas Radivoyevitch,
Roles Formal analysis, Writing – review & editing
Affiliation Department of Quantitative Health Sciences, Cleveland Clinic, Cleveland, Ohio, United States of America
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Daisy Pacelli,
Roles Project administration, Supervision, Validation, Writing – review & editing
Affiliation Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America
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Sherry Fada,
Roles Data curation, Project administration, Writing – review & editing
Affiliation Department of Hematology and Oncology, Taussig Cancer Institute, Cleveland Clinic, Cleveland, Ohio, United States of America
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Matthew Rump,
Roles Data curation, Software, Writing – review & editing
Affiliation Department of Hematology and Oncology, Taussig Cancer Institute, Cleveland Clinic, Cleveland, Ohio, United States of America
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Matthew Hsieh,
Roles Investigation, Writing – review & editing
Affiliation Molecular and Clinical Hematology Section, National Institutes of Health, Bethesda, Maryland, United States of America
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John F. Tisdale,
Roles Investigation, Writing – review & editing
Affiliation Molecular and Clinical Hematology Section, National Institutes of Health, Bethesda, Maryland, United States of America
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James Jacobberger,
Roles Formal analysis, Methodology, Writing – review & editing
Affiliation Case Comprehensive Cancer Center, Case Western Reserve University, Cleveland, Ohio, United States of America
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Mitch Phelps,
Roles Formal analysis, Methodology, Writing – review & editing
Affiliation College of Pharmacy, The Ohio State University, Columbus, Ohio, United States of America
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James Douglas Engel,
Roles Investigation, Writing – review & editing
Affiliation Cell and Developmental Biology, University of Michigan, Ann Arbor, Michigan, United States of America
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Santhosh Saraf,
Roles Investigation, Supervision, Writing – review & editing
Affiliation Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America
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Lewis L. Hsu,
Roles Investigation, Writing – review & editing
Affiliation Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America
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Victor Gordeuk,
Roles Investigation, Writing – review & editing
Affiliation Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America
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Joseph DeSimone,
Roles Conceptualization, Funding acquisition, Methodology, Project administration, Writing – review & editing
Affiliation Department of Medicine, University of Illinois Hospital and Health Sciences System, Chicago, Illinois, United States of America
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Yogen Saunthararajah
Roles Conceptualization, Formal analysis, Funding acquisition, Investigation, Methodology, Project administration, Resources, Writing – original draft, Writing – review & editing
* E-mail: saunthy@ccf.org
Affiliations Translational Hematology and Oncology Research, Taussig Cancer Institute, Cleveland Clinic, Cleveland, Ohio, United States of America, Department of Hematology and Oncology, Taussig Cancer Institute, Cleveland Clinic, Cleveland, Ohio, United States of America
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Oral tetrahydrouridine and decitabine for non-cytotoxic epigenetic gene regulation in sickle cell disease: A randomized phase 1 study
- Robert Molokie,
- Donald Lavelle,
- Michel Gowhari,
- Michael Pacini,
- Lani Krauz,
- Johara Hassan,
- Vinzon Ibanez,
- Maria A. Ruiz,
- Kwok Peng Ng,
- Philip Woost
- Published: September 7, 2017
- https://doi.org/10.1371/journal.pmed.1002382