Lentiviral Gene Transfer of Rpe65 Rescues Survival and Function of Cones in a Mouse Model of Leber Congenital Amaurosis

• Alexis-Pierre Bemelmans ,

  Contributed equally to this work with: Alexis-Pierre Bemelmans, Corinne Kostic

  Affiliation Unit of Gene Therapy and Stem Cell Biology, Jules Gonin Eye Hospital, Lausanne, Switzerland

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• Corinne Kostic ,

  Contributed equally to this work with: Alexis-Pierre Bemelmans, Corinne Kostic

  Affiliation Unit of Gene Therapy and Stem Cell Biology, Jules Gonin Eye Hospital, Lausanne, Switzerland

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• Sylvain V Crippa,

  Affiliation Unit of Gene Therapy and Stem Cell Biology, Jules Gonin Eye Hospital, Lausanne, Switzerland

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• William W Hauswirth,

  Affiliation Department of Ophthalmology, University of Florida, Gainesville, Florida, United States of America

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• Janis Lem,

  Affiliation Department of Ophthalmology, Program in Genetics and Tufts Center for Vision Research, Tufts University School of Medicine, Boston, Massachusetts, United States of America

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• Francis L Munier,

  Affiliation Unit of Clinical Oculogenetics, Jules Gonin Eye Hospital, Lausanne, Switzerland

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• Mathias W Seeliger,

  Affiliation Retinal Electrodiagnostics Research Group, Department of Ophthalmology II, Eberhard-Karls University, Tübingen, Germany

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• Andreas Wenzel,

  Affiliation Laboratory of Retinal Cell Biology, University Hospital, Zürich, Switzerland

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• Yvan Arsenijevic

  *To whom correspondence should be addressed. E-mail: yvan.arsenijevic@ophtal.vd.ch

  Affiliation Unit of Gene Therapy and Stem Cell Biology, Jules Gonin Eye Hospital, Lausanne, Switzerland

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