About the Authors
- Alain Fischer
-
*To whom correspondence should be addressed. E-mail: alain.fischer@nck.ap-hop-paris.fr
- Pascale Borensztein
- Claire Roussel
Competing Interests
The academic and pharmaceutical partners that support the European Rare Diseases Therapeutic Initiative are specified at http://www.erditi.org. AF is on the editorial board of PLoS Medicine.