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Open Access
Peer-reviewed
Research Article
Functional screening of lysosomal storage disorder genes identifies modifiers of alpha-synuclein neurotoxicity
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Meigen Yu,
Roles Conceptualization, Formal analysis, Investigation, Writing – original draft, Writing – review & editing
Affiliation Department of Neuroscience, Baylor College of Medicine, Houston, Texas, United States of America
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Hui Ye,
Roles Investigation, Writing – review & editing
Affiliation Department of Neurology, Baylor College of Medicine, Houston, Texas, United States of America
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Ruth B. De-Paula,
Roles Formal analysis, Investigation, Writing – review & editing
Affiliation Quantitative and Computational Biology Program, Baylor College of Medicine, Houston, Texas, United States of America
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Carl Grant Mangleburg,
Roles Formal analysis, Software, Visualization, Writing – review & editing
Affiliations Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, Texas, United States of America, Medical Scientist Training Program, Baylor College of Medicine, Houston, Texas, United States of America
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Timothy Wu,
Roles Formal analysis, Software, Visualization
Affiliations Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, Texas, United States of America, Medical Scientist Training Program, Baylor College of Medicine, Houston, Texas, United States of America
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Tom V. Lee,
Roles Investigation, Validation, Writing – review & editing
Affiliation Department of Neurology, Baylor College of Medicine, Houston, Texas, United States of America
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Yarong Li,
Roles Investigation, Writing – review & editing
Affiliation Department of Neurology, Baylor College of Medicine, Houston, Texas, United States of America
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Duc Duong,
Roles Conceptualization, Data curation, Investigation, Writing – review & editing
Affiliation Departments of Biochemistry and Neurology, Emory University School of Medicine, Atlanta, Georgia, United States of America
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Bridget Phillips,
Roles Formal analysis, Investigation, Visualization, Writing – review & editing
Affiliations Department of Psychiatry, Washington University, St. Louis, Missouri, United States of America, NeuroGenomics and Informatics, Washington University, St. Louis, Missouri, United States of America
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Carlos Cruchaga,
Roles Investigation, Supervision, Writing – review & editing
Affiliations Department of Psychiatry, Washington University, St. Louis, Missouri, United States of America, NeuroGenomics and Informatics, Washington University, St. Louis, Missouri, United States of America
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Genevera I. Allen,
Roles Formal analysis, Methodology, Software, Writing – review & editing
Affiliations Departments of Electrical and Computer Engineering, Computer Science, and Statistics, Rice University, Houston, Texas, United States of America, Jan and Dan Duncan Neurological Research Institute, Texas Children’s Hospital, Houston, Texas, United States of America
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Nicholas T. Seyfried,
Roles Conceptualization, Funding acquisition, Resources, Supervision, Writing – review & editing
Affiliation Departments of Biochemistry and Neurology, Emory University School of Medicine, Atlanta, Georgia, United States of America
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Ismael Al-Ramahi,
Roles Conceptualization, Methodology, Supervision, Writing – review & editing
Affiliations Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, Texas, United States of America, Jan and Dan Duncan Neurological Research Institute, Texas Children’s Hospital, Houston, Texas, United States of America, Center for Alzheimer’s and Neurodegenerative Diseases, Baylor College of Medicine, Houston, Texas, United States of America
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Juan Botas,
Roles Conceptualization, Funding acquisition, Investigation, Methodology, Resources, Supervision, Writing – review & editing
Affiliations Quantitative and Computational Biology Program, Baylor College of Medicine, Houston, Texas, United States of America, Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, Texas, United States of America, Jan and Dan Duncan Neurological Research Institute, Texas Children’s Hospital, Houston, Texas, United States of America, Center for Alzheimer’s and Neurodegenerative Diseases, Baylor College of Medicine, Houston, Texas, United States of America
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Joshua M. Shulman
Roles Conceptualization, Funding acquisition, Investigation, Resources, Supervision, Writing – original draft, Writing – review & editing
* E-mail: Joshua.Shulman@bcm.edu
Affiliations Department of Neuroscience, Baylor College of Medicine, Houston, Texas, United States of America, Department of Neurology, Baylor College of Medicine, Houston, Texas, United States of America, Department of Molecular and Human Genetics, Baylor College of Medicine, Houston, Texas, United States of America, Jan and Dan Duncan Neurological Research Institute, Texas Children’s Hospital, Houston, Texas, United States of America, Center for Alzheimer’s and Neurodegenerative Diseases, Baylor College of Medicine, Houston, Texas, United States of America
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Functional screening of lysosomal storage disorder genes identifies modifiers of alpha-synuclein neurotoxicity
- Meigen Yu,
- Hui Ye,
- Ruth B. De-Paula,
- Carl Grant Mangleburg,
- Timothy Wu,
- Tom V. Lee,
- Yarong Li,
- Duc Duong,
- Bridget Phillips,
- Carlos Cruchaga
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- Published: May 18, 2023
- https://doi.org/10.1371/journal.pgen.1010760