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Evaluation of Aminoglycoside and Non-Aminoglycoside Compounds for Stop-Codon Readthrough Therapy in Four Lysosomal Storage Diseases
- Marta Gómez-Grau,
- Elena Garrido,
- Mónica Cozar,
- Víctor Rodriguez-Sureda,
- Carmen Domínguez,
- Concepción Arenas,
- Richard A. Gatti,
- Bru Cormand,
- Daniel Grinberg,
- Lluïsa Vilageliu
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- Published: August 19, 2015
- https://doi.org/10.1371/journal.pone.0135873