-
Loading metrics
Long-Term Efficacy, Safety, and Pharmacokinetics of Drisapersen in Duchenne Muscular Dystrophy: Results from an Open-Label Extension Study
- Nathalie M. Goemans,
- Már Tulinius,
- Marleen van den Hauwe,
- Anna-Karin Kroksmark,
- Gunnar Buyse,
- Rosamund J. Wilson,
- Judith C. van Deutekom,
- Sjef J. de Kimpe,
- Afrodite Lourbakos,
- Giles Campion
x
- Published: September 2, 2016
- https://doi.org/10.1371/journal.pone.0161955