About the Authors

Jeffrey S. Smith

Affiliation Division of Cellular and Gene Therapies, Food and Drug Administration Center for Biologics Evaluation and Research, Bethesda, Maryland, United States of America

Zhili Xu

Affiliation Division of Cellular and Gene Therapies, Food and Drug Administration Center for Biologics Evaluation and Research, Bethesda, Maryland, United States of America

Jie Tian

Affiliation Division of Cellular and Gene Therapies, Food and Drug Administration Center for Biologics Evaluation and Research, Bethesda, Maryland, United States of America

Donna J. Palmer

Affiliation Molecular and Human Genetics, Baylor College of Medicine, Houston, Texas, United States of America

Philip Ng

Affiliation Molecular and Human Genetics, Baylor College of Medicine, Houston, Texas, United States of America

Andrew P. Byrnes

andrew.byrnes@fda.hhs.gov

Affiliation Division of Cellular and Gene Therapies, Food and Drug Administration Center for Biologics Evaluation and Research, Bethesda, Maryland, United States of America

Competing Interests

The authors have declared that no competing interests exist.

Author Contributions

Conceived and designed the experiments: JSS APB. Performed the experiments: JSS ZX. Analyzed the data: JSS APB. Contributed reagents/materials/analysis tools: DJP PN. Wrote the paper: JSS APB. Produced viruses: JT DJP PN.