About the Authors
- Alfredo D. Guerron
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Rashmi Rawat
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Arpana Sali
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Christopher F. Spurney
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Affiliation Division of Cardiology, Children's National Medical Center, Washington, D. C., United States of America
- Emidio Pistilli
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Affiliation Pennsylvania Muscle Institute, University of Pennsylvania, Philadelphia, Pennsylvania, United States of America
- Hee-Jae Cha
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Affiliation Department of Parasitology and Genetics, Kosin University College of Medicine, Pusan, South Korea
- Gouri S. Pandey
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Ramkishore Gernapudi
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Dwight Francia
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Viken Farajian
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Diana M. Escolar
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Laura Bossi
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Affiliation Transgene SA, Illkirch-Graffenstaden, France
- Magali Becker
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Affiliation Transgene SA, Illkirch-Graffenstaden, France
- Patricia Zerr
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Affiliation Transgene SA, Illkirch-Graffenstaden, France
- Sabine de la Porte
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Affiliation Laboratoire de Neurobiologie Cellulaire et Moléculaire, Institut Fédératif de Neurobiologie Alfred Fessard, Cedex, France
- Heather Gordish-Dressman
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Terence Partridge
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Eric P. Hoffman
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Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
- Kanneboyina Nagaraju
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* E-mail: knagaraju@cnmcresearch.org
Affiliation Center for Genetic Medicine Research, Children's National Medical Center, Department of Integrative Systems Biology, George Washington University School of Medicine and Health Sciences, Washington, D. C., United States of America
Competing Interests
This study was done by the preclinical drug testing facility as a fee-per service agreement. Laura Bossi, Megali Becker and Patricia Zerr are affiliated with Faust Pharmaceuticals. This does not alter the authors' adherence to all the PLOS one policies on sharing data and materials.
Author Contributions
Conceived and designed the experiments: DE EH KN. Performed the experiments: ADG RR AS CFS HJC GP RG DF VF EEP TP. Analyzed the data: ADG RR AS CFS LB MB PZ SdlP HGD DE EH TP KN. Contributed reagents/materials/analysis tools: AS TP. Wrote the paper: ADG HGD TP KN.